Orphan Drugs Market

Global Orphan Drugs Market Size, Trends & Analysis - Forecasts to 2028 By Drug Type (Biological and Non-Biological), By Disease Type (Oncologic Diseases, Metabolic Diseases, Hematologic and Immunologic Diseases, Infectious Diseases, and Others), By Therapy Class (Oncology, Hematology, Neurology, and Others), By Distribution Channel (Hospital Pharmacy, Retail Pharmacy, Online Sales, and Others) and By Region (North America, Asia Pacific, South America, Europe, and the Middle East and Africa), Competitive Landscape, Company Market Share Analysis, and Competitor Analysis

Category Healthcare
Format
  • ms word
  • ms excel
  • ms ppt
  • pdf
This report was recently updated on May 12 2024 with the latest and most recent market numbers

Global Orphan Drugs Market Size

The global orphan drugs market is expected to grow from USD 201.5 Billion in 2023 to 454.8 Billion by 2028 and is projected to grow at a CAGR of 14.5% from 2023 to 2028.

An orphan drug is a pharmaceutical product that is used to treat rare disorders. An orphan drug is produced in order to target a small group of patients in the overall drugs market. This requires fewer marketing and advertising process since the targeted patients come under a smaller scale as compared other disease segments.

Most rare diseases are genetic in nature and are associated with the patient for the rest of their lives. Orphan drugs are used to treat these types of rare diseases which occur due to changes in the genes. In the report shared by the national institute of health (NIH) in 2020, there were an estimated 7000 rare diseases in the U.S., and approximately 25-30 million Americans are living with rare diseases. Because of the rising prevalence, the series of manufacturing FDA approved orphan drugs is increasing rapidly.

The favorable government guidelines for orphan drugs is expected to boost the market. Furthermore, the increasing prevalence of rare diseases and high treatment costs per patient fuels the global orphan drugs market. In addition, increasing cancer and genetic diseases drive the growth of the market. Moreover, increasing awareness about the benefits of orphan drugs and increasing investment in R&D initiatives are expected to act as growth-inducing factors for the orphan drugs market.

The requirement for rare diseases medicine and the availability of a market exclusively for drugs manufacturers is creating opportunities in the global orphan drugs market. The government policies and subsidiaries for rare disease medicine help emerging drugs manufacturers. In addition, extensive spending on research and development helps orphan drugs development.

global orphan drugs market

Global Orphan Drugs Market: By Drug Type

The biological segment is expected to be the fastest-growing segment in the market from 2023-2028. The presence of a platform and feature of delivery is the major growth factor of the biological segment, and because of that, this segment holds the largest share of the market. The food and drug administration (FDA) of the U.S., has developed over 600 orphan drugs and their designation.

Global Orphan Drugs Market: By Disease Type

The oncologic diseases segment holds the largest share of the global orphan drugs market and is anticipated to be the fastest-growing segment in the market from 2023-2028. The oncologic disease is the most common disease among all and it is classified into pancreatic cancer, ovarian cancer, and others. Metabolic diseases are related to the processing of food into energy. Hematologic diseases are related to blood and blood-producing organs which are most common in the U.S.

Global Orphan Drugs Market: By Therapy Type

The oncology segment holds the largest share of the global orphan drugs market and is anticipated to be the fastest-growing segment in the market from 2023-2028. The key players in the market are focusing on the production of oncology drugs and a large number of oncology drugs are used in the treatment of cancer. The hematology segment is the second most dominating segment because hematology products are increasing rapidly with fast positive regulatory approvals.

Global Orphan Drugs Market: By Distribution Channel

The online sales segment is expected to be the fastest-growing segment in the market from 2023-2028. In online sales, consumers can easily purchase a drug with their mobile or laptop devices which provides the best purchase experience. Hospital pharmacy holds the largest share of the market. In hospital pharmacy, drugs are provided by a trained healthcare professional. Retail pharmacy is expected to remain stable in the forecast period.

asia pacific orphan drugs market

Global Orphan Drugs Market: By Region

Geographically, the market is anticipated to remain stable in North America due to rising cases of rare diseases, better reimbursement policies, and a strong patient population. This region holds the largest share of the global orphan drugs market.

Asia Pacific is growing rapidly due to the competitive landscape. The growing healthcare infrastructure and increasing awareness about the disease is the major growth factor for this region.

The European orphan drugs market is dominated by France, Belgium, Italy, Germany, and United Kingdom. The presence of a strong patient population and the adoption of new drugs therapies are helping to register better CAGR in this region.

Global Orphan Drugs Market Share and Competitor Analysis

The key players covered in the global orphan drugs market are Amgen Inc., Bayer AG, F. Hoffmann-La Roche Ltd, Alexion Pharmaceutical Inc., Novo Nordisk A/S, Novartis AG, Bristol-Myers Squibb Company, AstraZeneca, Daiichi Sankyo Company, and GlaxoSmithKline plc, among others.

Please note: This is not an exhaustive list of companies profiled in the report.

Chapter 1   Research Methodology

1.1    Research Assumptions

1.2    Research Methodology

1.2.1    Estimates and Forecast Timeline

1.3    Information Procurement

1.3.1    Purchased Database

1.3.2    GME’s Internal Database

1.3.3    Primary Research

1.3.4    Secondary Sources & Third-Party Perspectives

            1.3.4.1    Company Information Sources: Annual Reports, Investor Presentation, Press Release, SEC Filing, Company Blogs & Website

           1.3.4.2 Secondary Data Sources: World Health Organization, Laboratory Corporation of America Holdings, IQVIA, Syneos Health

1.4    Information or Data Analysis

1.4.1    Data Analysis Models

1.5    Market Therapy Class & Data Visualization

1.6    Data Validation & Publishing

1.7   Market Model

1.7.1    Model Details

              1.7.1.1 Top-Down Approach

               1.7.1.2 Bottom-Up Approach

1.8    Market Segmentation & Scope

1.9    Market Definition

Chapter 2   Executive Summary

2.1.    Global Market Outlook

2.2     Drug Type Outlook

2.3     Disease Type Outlook

2.4     Therapy Class Outlook

2.5     Distribution Channel Outlook

2.6     Regional Outlook

Chapter 3   Global Orphan Drug Market Trend Analysis

3.1. Market Introduction

3.2 Penetration & Growth Prospect Mapping

3.3 Impact of COVID-19 on the Orphan Drug Market

3.4 Metric Data on Industry

3.5 Market Dynamic

3.5.1 Market Driver Analysis

3.5.2 Market Restraint Analysis

3.5.3 Industry Challenges

3.5.4 Industry Opportunities

3.6    Porter’s Five Analysis

3.6.1 Supplier Power

3.6.2 Buyer Power

3.6.3 Substitution Threat

3.6.4 Threat from New Entrant

3.7 Market Entry Strategies

Chapter 4   Orphan Drug Market: Drug Type Trend Analysis

4.1   Drug Type: Historic Data vs. Forecast Data Analysis, 2022 vs. 2028

4.2   Biological

4.2.1    Market Estimates & Forecast Analysis of Biological Segment, By Region, 2022-2028 (USD Billion)

4.3   Non-Biological

4.3.1    Market Estimates & Forecast Analysis of Non-Biological Markets Segment, By Region, 2022-2028 (USD Billion)

Chapter 5   Orphan Drug Market: Disease Type Trend Analysis

5.1    Disease Type: Historic Data vs. Forecast Data Analysis, 2022 vs. 2028

5.2    Oncologic Disease

5.2.1    Market Estimates & Forecast Analysis of Oncologic Disease Segment, By Region, 2022-2028 (USD Billion)

5.3     Metabolic Diseases

5.3.1    Market Estimates & Forecast Analysis of Metabolic Diseases Segment, By Region, 2022-2028 (USD Billion)

5.4     Hematologic and Immunologic Diseases

5.4.1    Market Estimates & Forecast Analysis of Hematologic and Immunologic Diseases Segment, By Region, 2022-2028 (USD Billion)

5.5     Infectious Diseases

5.5.1    Market Estimates & Forecast Analysis of Infectious Diseases Segment, By Region, 2022-2028 (USD Billion)

5.6     Others

          5.6.1    Market Estimates & Forecast Analysis of Others Segment, By Region, 2022-2028 (USD Billion)

Chapter 6   Orphan Drug Market: Therapy Class Trend Analysis

6.1    Therapy Class: Historic Data vs. Forecast Data Analysis, 2022 vs. 2028

6.2    Oncology

6.2.1    Market Estimates & Forecast Analysis of Oncology Segment, By Region, 2022-2028 (USD Billion)

6.3    Hematology

6.3.1    Market Estimates & Forecast Analysis of Hematology Segment, By Region, 2022-2028 (USD Billion)

6.4   Neurology

6.4.1    Market Estimates & Forecast Analysis of Neurology Segment, By Region, 2022-2028 (USD Billion)

6.5   Others

          6.5.1    Market Estimates & Forecast Analysis of Others Segment, By Region, 2022-2028 (USD Billion)

Chapter 7   Orphan Drug Market: Distribution Channel Trend Analysis

7.1   Distribution Channel: Historic Data vs. Forecast Data Analysis, 2022 vs. 2028

7.2    Hospital Pharmacy

7.2.1    Market Estimates & Forecast Analysis of Hospital Pharmacy Segment, By Region, 2022-2028 (USD Billion)

7.3    Retail Pharmacy

7.3.1    Market Estimates & Forecast Analysis of Retail Pharmacy Segment, By Region, 2022-2028 (USD Billion)

7.4    Online Sales

7.4.1    Market Estimates & Forecast Analysis of Online Sales Segment, By Region, 2022-2028 (USD Billion)

7.5    Others

7.5.1    Market Estimates & Forecast Analysis of Others Segment, By Region, 2022-2028 (USD Billion)

Chapter 9   Orphan Drug Market, By Region

8.1    Regional Outlook

8.2    North America

8.2.1    Market Estimates & Forecast Analysis, By Country 2022-2028(USD Billion)

8.2.2    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.2.3    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.2.4    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.2.5    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.2.6    U.S.

8.2.6.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.2.6.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.2.6.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.2.6.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.2.7    Canada

8.2.7.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.2.7.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.2.7.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.2.7.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.2.8    Mexico

8.2.8.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028 (USD Billion)

8.2.8.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028 (USD Billion)

8.2.8.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028 (USD Billion)

8.2.8.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3    Europe

8.3.1    Market Estimates & Forecast Analysis, By Country 2022-2028(USD Billion)

8.3.2    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.3    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.4    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.5    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.6    Germany

8.3.6.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.6.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.6.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.6.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.7    UK

8.3.7.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.7.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.7.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.7.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.8    France

8.3.8.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.8.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.8.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.8.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.9    Russia

8.3.9.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.9.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.9.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.9.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.10    Italy

8.3.10.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.10.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.10.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.10.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.11    Spain

8.3.11.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.3.11.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.3.11.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.3.11.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.3.12    Rest of Europe

8.3.12.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028 (USD Billion)

8.3.12.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028 (USD Billion)

8.3.12.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028 (USD Billion)

8.3.12.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4    Asia Pacific

8.4.1    Market Estimates & Forecast Analysis, By Country 2022-2028(USD Billion)

8.4.2    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.3    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.4    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.5    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.6    China

8.4.6.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.6.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.6.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.6.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.7    India

8.4.7.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.7.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.7.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.7.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.8    Japan

8.4.8.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.8.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.8.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.8.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.9    Australia

8.4.9.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.9.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.9.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.9.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.10    South Korea

8.4.10.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.4.10.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.4.10.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.4.10.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.4.11    Rest of Asia Pacific

8.4.11.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028 (USD Billion)

8.4.11.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028 (USD Billion)

8.4.11.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028 (USD Billion)

8.4.11.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.5    Central & South America

8.5.1    Market Estimates & Forecast Analysis, By Country 2022-2028(USD Billion)

8.5.2    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.5.3    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.5.4   Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.5.5   Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.5.6    Brazil

8.5.6.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.5.6.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.5.6.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.5.6.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.5.7    Rest of Central & South America

8.5.7.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.5.7.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.5.7.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.5.7.4    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.6    Middle East & Africa

8.6.1    Market Estimates & Forecast Analysis, By Country 2022-2028(USD Billion)

8.6.2    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.6.3    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.6.4    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.6.5    Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.6.6    Saudi Arabia

8.6.6.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.6.6.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.6.6.3   Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.6.6.4   Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.6.7    United Arab Emirates

8.6.7.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.6.7.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.6.7.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.6.7.4   Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.6.8    South Africa

8.6.8.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028(USD Billion)

8.6.8.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028(USD Billion)

8.6.8.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028(USD Billion)

8.6.8.4   Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

8.6.9   Rest of Middle East & Africa

8.6.9.1    Market Estimates & Forecast Analysis, By Drug Type, 2022-2028 (USD Billion)

8.6.9.2    Market Estimates & Forecast Analysis, By Disease Type, 2022-2028 (USD Billion)

8.6.9.3    Market Estimates & Forecast Analysis, By Therapy Class, 2022-2028 (USD Billion)

8.6.9.4   Market Estimates & Forecast Analysis, By Distribution Channel, 2022-2028(USD Billion)

Chapter 9   Competitive Analysis

9.1    Key Global Players, Recent Developments & their Impact on the Industry

9.2    Four Quadrant Competitor Positioning Matrix

9.2.1    Key Innovators

9.2.2    Market Leaders

9.2.3    Emerging Players

9.2.4    Market Challengers

9.3    Vendor Landscape Analysis

9.4    Distribution Channel Landscape Analysis

9.5    Company Market Share Analysis, 2022

Chapter 10   Company Profile Analysis

10.1    Amgen Inc.

10.1.1    Company Overview

10.1.2    Financial Analysis

10.1.3    Strategic Initiatives

10.1.4    Drug Type Benchmarking

10.2    Bayer AG

10.2.1    Company Overview

10.2.2    Financial Analysis

10.2.3    Strategic Initiatives

10.2.4    Drug Type Benchmarking

10.3     F. Hoffmann-La Roche Ltd

10.3.1    Company Overview

10.3.2    Financial Analysis

10.3.3    Strategic Initiatives

10.3.4    Drug Type Benchmarking

10.4    Alexion Pharmaceutical Inc.

10.4.1    Company Overview

10.4.2    Financial Analysis

10.4.3    Strategic Initiatives

10.4.4    Drug Type Benchmarking

10.5    Novo Nordisk A/S

10.5.1    Company Overview

10.5.2    Financial Analysis

10.5.3    Strategic Initiatives

10.5.4    Drug Type Benchmarking

10.6     Novartis AG

10.6.1    Company Overview

10.6.2    Financial Analysis

10.6.3    Strategic Initiatives

10.6.4    Drug Type Benchmarking

10.7    Bristol-Myers Squibb Company

10.7.1    Company Overview

10.7.2    Financial Analysis

10.7.3    Strategic Initiatives

10.7.4    Drug Type Benchmarking

10.8    AstraZeneca

10.8.1    Company Overview

10.8.2    Financial Analysis

10.8.3    Strategic Initiatives

10.8.4    Drug Type Benchmarking

10.9   Daiichi Sankyo Company

10.9.1    Company Overview

10.9.2    Financial Analysis

10.9.3    Strategic Initiatives

10.9.4    Drug Type Benchmarking

10.10   GlaxoSmithKline plc

10.10.1    Company Overview

10.10.2    Financial Analysis

10.10.3    Strategic Initiatives

10.10.4    Drug Type Benchmarking

10.11   Other Companies

10.11.1    Company Overview

10.11.2    Financial Analysis

10.11.3    Strategic Initiatives

10.11.4    Drug Type Benchmarking

List of Tables

1 Technological Advancements In Orphan Drug Market

2 Global Orphan Drug Market: Key Market Drivers

3 Global Orphan Drug Market: Key Market Challenges

4 Global Orphan Drug Market: Key Market Opportunities

5 Global Orphan Drug Market: Key Market Restraints

6 Global Orphan Drug Market Estimates & Forecast Analysis, 2022-2028 (USD Billion)

7 Global Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

8 Biological: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

9 Non-Biological: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

10 Global Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

11 Oncologic Diseases: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

12 Metabolic Diseases: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

13 Hematologic and Immunologic Diseases: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

14 Infectious Diseases: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

15 Others: Global Drug Market, By Region, 2022-2028 (USD Billion)

16 Global Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

17 Oncology: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

18 Hematology: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

19 Neurology: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

20 Others: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

21 Global Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

22 Hospital Pharmacy: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

23 Retail Pharmacy: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

24 Online Sales: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

25 Others: Global Orphan Drug Markey, By Region, 2022-2028 (USD billion)

26 Regional Analysis: Global Orphan Drug Market, By Region, 2022-2028 (USD Billion)

27 North America: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

28 North America: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

29 North America: Orphan Drug Market, By Therapy Class , 2022-2028 (USD Billion)

30 North America: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

31 North America: Orphan Drug Market, By Country, 2022-2028 (USD Billion)

32 U.S: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

33 U.S: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

34 U.S: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

35 U.S: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

36 Canada: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

37 Canada: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

38 Canada: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

39 Canada: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

40 Mexico: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

41 Mexico: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

42 Mexico: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

43 Mexico: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

44 Europe: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

45 Europe: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

46 Europe: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

47 Europe: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

48 Germany: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

49 Germany: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

50 Germany: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

51 Germany: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

52 UK: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

53 UK: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

54 UK: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

55 UK: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

56 France: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

57 France: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

58 France: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

59 France: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

60 Italy: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

61 Italy: Orphan Drug Market, By T Disease Type , 2022-2028 (USD Billion)

62 Italy: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

63 ltaly: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

64 Spain: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

65 Spain: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

66 Spain: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

67 Spain: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

68 Rest Of Europe: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

69 Rest Of Europe: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

70 Rest Of Europe: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

71 Rest of Europe: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

72 Asia Pacific: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

73 Asia Pacific: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

74 Asia Pacific: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

75 Asia Pacific: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

76 Asia Pacific: Orphan Drug Market, By Country, 2022-2028 (USD Billion)

77 China: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

78 China: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

79 China: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

80 China: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

81 India: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

82 India: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

83 India: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

84 India: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

85 Japan: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

86 Japan: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

87 Japan: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

88 Japan: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

89 South Korea: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

90 South Korea: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

91 South Korea: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

92 South Korea: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

93 Middle East & Africa: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

94 Middle East & Africa: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

95 Middle East & Africa: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

96 Middle East & Africa: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

97 Middle East & Africa: Orphan Drug Market, By Country, 2022-2028 (USD Billion)

98 Saudi Arabia: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

99 Saudi Arabia: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

100 Saudi Arabia: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

101 Saudi Arabia: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

102 UAE: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

103 UAE: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

104 UAE: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

105 UAE: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

106 Central & South America: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

107 Central & South America: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

108 Central & South America: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

109 Central & South America: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

110 Central & South America: Orphan Drug Market, By Country, 2022-2028 (USD Billion)

111 Brazil: Orphan Drug Market, By Drug Type, 2022-2028 (USD Billion)

112 Brazil: Orphan Drug Market, By Disease Type, 2022-2028 (USD Billion)

113 Brazil: Orphan Drug Market, By Therapy Class, 2022-2028 (USD Billion)

114 Brazil: Orphan Drug Market, By Distribution Channel, 2022-2028 (USD Billion)

115 Amgen Inc.: Drug Types Offered

116 Bayer AG: Drug Types Offered

117 F. Hoffmann-La Roche Ltd: Drug Types Offered

118 Alexion Pharmaceutical Inc.: Drug Types Offered

119 Novo Nordisk A/S: Drug Types Offered

120 Novartis AG: Drug Types Offered

121 Bristol-Myers Squibb Company: Drug Types Offered

122 AstraZeneca: Drug Types Offered

123 Daiichi Sankyo Company: Drug Types Offered

124 GlaxoSmithKline plc: Drug Types Offered

125 Analog Devices, Inc: Drug Types Offered

126 Other Companies: Drug Types Offered

List of Figures

1. Global Orphan Drug Market Segmentation & Research Scope

2. Primary Research Partners and Local Informers

3. Primary Research Process

4. Primary Research Approaches

5. Primary Research Responses

6. Global Orphan Drug Market: Penetration & Growth Prospect Mapping

7. Global Orphan Drug Market: Value Chain Analysis

8. Global Orphan Drug Market Drivers

9. Global Orphan Drug Market Restraints

10. Global Orphan Drug Market Opportunities

11. Global Orphan Drug Market Challenges

12. Key Orphan Drug Market Manufacturer Analysis

13. Global Orphan Drug Market: Porter’s Five Forces Analysis

14. PESTLE Analysis & Impact Analysis

15. Amgen Inc.: Company Snapshot

16. Amgen Inc.: Swot Analysis

17. Bayer AG: Company Snapshot

18. Bayer AG: Swot Analysis

19. F. Hoffmann-La Roche Ltd: Company Snapshot

20. F. Hoffmann-La Roche Ltd: Swot Analysis

21. Alexion Pharmaceutical Inc.: Company Snapshot

22. Alexion Pharmaceutical Inc.: Swot Analysis

23. Novo Nordisk A/S: Company Snapshot

24. Novo Nordisk A/S: Swot Analysis

25. Novartis AG: Company Snapshot

26. Novartis AG: Swot Analysis

27. Bristol-Myers Squibb Company: Company Snapshot

28. Bristol-Myers Squibb Company: Swot Analysis

29. ASTRAZENECA: Company Snapshot

30. ASTRAZENECA: Swot Analysis

31. Daiichi Sankyo Company: Company Snapshot

32. Daiichi Sankyo Company: Swot Analysis

33. Enchandia AB Software: Company Snapshot

34. Enchandia AB Software: Swot Analysis

35. GlaxoSmithKline plc: Company Snapshot

36. GlaxoSmithKline plc: Swot Analysis

37. Analog Devices, Inc: Company Snapshot

38. Analog Devices, Inc: Swot Analysis

39. Other Companies: Company Snapshot

40. Other Companies: Swot Analysis

The Global Orphan Drugs Market has been studied from the year 2019 till 2028. However, the CAGR provided in the report is from the year 2023 to 2028. The research methodology involved three stages: Desk research, Primary research, and Analysis & Output from the entire research process.

The desk research involved a robust background study which meant referring to paid and unpaid databases to understand the market dynamics; mapping contracts from press releases; identifying the key players in the market, studying their product portfolio, competition level, annual reports/SEC filings & investor presentations; and learning the demand and supply-side analysis for the Orphan Drugs Market.

The primary research activity included telephonic conversations with more than 50 tier 1 industry consultants, distributors, and end-use product manufacturers.

Finally, based on the above thorough research process, an in-depth analysis was carried out considering the following aspects: market attractiveness, current & future market trends, market share analysis, SWOT analysis of the company and customer analytics.

We value your investment and offer free customization with every report to fulfil your exact research needs.
This website is secure and your personal details are safe. Privacy
You can also purchase parts of this report. Do you want to check out a section wise price list?

Frequently Asked Questions

The global orphan drug market is expected to grow from USD 201.5 Billion in 2023 to 454.8 Billion by 2028 and is projected to grow at a CAGR of 14.5% from 2023 to 2028.
Amgen Inc., Bayer AG, F. Hoffmann-La Roche Ltd, Alexion Pharmaceutical Inc., Novo Nordisk A/S, Novartis AG, Bristol-Myers Squibb Company, AstraZeneca, Daiichi Sankyo Company, and GlaxoSmithKline plc, among others are the top vendors in the market.
The rising demand for treatment drugs and medicines for rare diseases and rising number of players in the space exclusively for orphan drug manufacturing are some of the factors that are creating opportunities in the global orphan drug market.
Increasing awareness about the benefits of orphan drugs and increasing investment in R&D initiatives are expected to act as growth-inducing factors for the orphan drugs market.

Tailor made solutions just for you

80% of our clients seek made-to-order reports. How do you want us to tailor yours?

OUR CLIENTS

  • Client of Global Market Estimates - Fedex
  • Client of Global Market Estimates - Samsung
  • Client of Global Market Estimates - Siemens
  • Client of Global Market Estimates - Lonza
  • Client of Global Market Estimates - DuPont
  • Client of Global Market Estimates - Medtronic
  • Client of Global Market Estimates - Toray
  • Client of Global Market Estimates - Signify
  • Client of Global Market Estimates - Teledyne
  • Client of Global Market Estimates - Trelleborg
  • Client of Global Market Estimates - Kikkoman Biochemifa
  • Client of Global Market Estimates - Leoni
  • Client of Global Market Estimates - Molnlycke
  • Client of Global Market Estimates - Spirent
  • Client of Global Market Estimates - Tokyo Electron Limited
  • Client of Global Market Estimates - Aranca
  • Client of Global Market Estimates - Asahi Kasei
  • Client of Global Market Estimates - Chimai
  • Client of Global Market Estimates - Grapsud
  • Client of Global Market Estimates - Horiba
  • Client of Global Market Estimates - Indorama
  • Client of Global Market Estimates - L&T
  • Client of Global Market Estimates - Integralife
  • Client of Global Market Estimates - Synamedia
  • Client of Global Market Estimates - Sorrento Therapeutics
  • Client of Global Market Estimates - Solenis
  • Client of Global Market Estimates - Sartorius